Project Title: |
Study Evaluating Patients With Cystinuria |
Project Type: |
Clinical Trial, Enrolment ongoing |
Disease group(s): |
Tubulopathies |
Project Summary: |
This is an open label, multicentre study, evaluating the safety, tolerability, efficacy, compliance and acceptability of alkalising treatments at long-term in patients with cystinuria. |
Lead principal investigator(s): |
Bertrand Knebelmann, Paris |
Co-investigator(s): |
Myriam Dao, Paris |
Project Period: |
02/2019 - 08/2022 |
Sponsors: |
Industry |
ClinicalTrials.gov: |
NCT04137978 |