Research Project

Project Title:

Study Evaluating Patients With Cystinuria

Project Type:

Clinical Trial, Enrolment ongoing

Disease group(s):

Tubulopathies

Project Summary:

This is an open label, multicentre study, evaluating the safety, tolerability, efficacy, compliance and acceptability of alkalising treatments at long-term in patients with cystinuria.

Lead principal investigator(s):

Bertrand Knebelmann, Paris

Co-investigator(s):

Myriam Dao, Paris

Project Period:

02/2019   -   08/2022

Sponsors:

Industry

ClinicalTrials.gov:

NCT04137978

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