Project Title: |
Novel molecular therapies for cystinosis |
Project Type: |
Translational research |
Disease group(s): |
Metabolic & stone disorders |
Project Summary: |
In this pre-clinical project we test gene and mRNA-based therapies for cystinosis. |
Lead principal investigator(s): |
Elena Levtchenko, Amsterdam |
Co-investigator(s): |
Rik Gijbers, Leuven Roland Brock, Nijmegen Lambertus van den Heuvel, Leuven |
Project Period: |
01/2018 - 01/2024 |
Sponsors: |
Non-profit foundation, National funding agency, Local resources |